AB1

Sickle Cell Disease

Pre-clinicalActive

Key Facts

Indication
Sickle Cell Disease
Phase
Pre-clinical
Status
Active
Company

About AkiraBio

AkiraBio is a private, preclinical-stage biotech targeting hemoglobinopathies with its lead candidate, AB1. AB1 is an oral, once-daily small molecule designed to induce fetal hemoglobin (HbF) production by inhibiting DNMT1, aiming to act as a 'functional cure' for sickle cell disease and thalassemia. The company is positioned in a high-need market with significant unmet medical need, seeking to develop a convenient, broadly accessible therapy. As a young company, it is pre-revenue and focused on advancing its lead program through clinical development.

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