Apriligen

Apriligen

Pre-clinical
San Diego, United StatesFounded 2021apriligen.com

Dedicated to curing rare pediatric diseases caused by the failure of a single gene beginning with our first clinical gene therapy program, APR-2020 – a purpose built lentiviral vector to treat RPS-19 Deficient Diamond Blackfan Anemia (“DBA”).

Founded
2021
Focus
Viral Technology

About

Dedicated to curing rare pediatric diseases caused by the failure of a single gene beginning with our first clinical gene therapy program, APR-2020 – a purpose built lentiviral vector to treat RPS-19 Deficient Diamond Blackfan Anemia (“DBA”).

Company Info

TypePrivate
Founded2021
LocationSan Diego, United States
StagePre-clinical
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