Apellis Pharmaceuticals

Apellis Pharmaceuticals

APLSApproved

Apellis Pharmaceuticals is a commercial-stage biopharma company focused on developing first-in-class therapies by targeting C3, the central protein of the complement system. The company has successfully brought two medicines to market—SYFOVRE® (pegcetacoplan) for geographic atrophy and EMPAVELI® (pegcetacoplan) for PNH—addressing significant unmet needs in ophthalmology and hematology. With a deep pipeline exploring C3 inhibition across rare, retinal, and neurological diseases, Apellis leverages over two decades of complement expertise to pursue life-changing treatments. The company operates with a culture of courageous science and compassion, driven by its founding scientific team.

Market Cap
$2.2B
Focus
RNA & Gene Therapy

APLS · Stock Price

USD 17.2132.07 (-65.08%)

Historical price data

AI Company Overview

Apellis Pharmaceuticals is a commercial-stage biopharma company focused on developing first-in-class therapies by targeting C3, the central protein of the complement system. The company has successfully brought two medicines to market—SYFOVRE® (pegcetacoplan) for geographic atrophy and EMPAVELI® (pegcetacoplan) for PNH—addressing significant unmet needs in ophthalmology and hematology. With a deep pipeline exploring C3 inhibition across rare, retinal, and neurological diseases, Apellis leverages over two decades of complement expertise to pursue life-changing treatments. The company operates with a culture of courageous science and compassion, driven by its founding scientific team.

Technology Platform

Targeted C3 therapy platform designed to comprehensively control the complement cascade by inhibiting the central protein C3, which addresses all three pathways of complement activation.

Pipeline Snapshot

27

27 drugs in pipeline, 11 in Phase 3

DrugIndicationStageWatch
APL-2 + APL-2Geographic AtrophyPhase 3
PegcetacoplanC3GPhase 3
APL-2 + APL-2Geographic AtrophyPhase 3
APL-2, PegcetacoplanGeographic Atrophy Secondary to Age-related Macular DegenerationPhase 3
APL-2Paroxysmal Nocturnal HemoglobinuriaPhase 3

FDA Approved Drugs

2
SYFOVRENDAFeb 17, 2023
EMPAVELINDAMay 14, 2021

Opportunities

Significant growth opportunities exist from the ongoing launch of SYFOVRE in the large, untreated GA market and expansion of pegcetacoplan into new indications like C3G/IC-MPGN and ALS.
The company's deep C3 expertise also provides a platform for developing next-generation therapies for a wider range of complement-mediated diseases.

Risk Factors

Key risks include commercial execution challenges for SYFOVRE amid competition and safety monitoring, clinical trial failures in ongoing Phase 3/2 studies, and the financial pressure of operating at a net loss while funding commercial and R&D activities.
The competitive landscape in complement inhibition is intensifying.

Competitive Landscape

Apellis faces competition from Astellas/Iveric Bio's IZERVAY in GA and from Alexion/AstraZeneca's Soliris/Ultomiris and Novartis's Fabhalta in PNH. Its differentiation is based on its first-in-class C3 inhibition platform, which offers a broader mechanism of action targeting the central node of the complement cascade.

Publications
15
Patents
20
Pipeline
27
FDA Approvals
2

Company Info

TypeTherapeutics
LocationUnited States
StageApproved
RevenueRevenue Generating

Trading

TickerAPLS
ExchangeNASDAQ

Therapeutic Areas

HematologyOphthalmologyNephrologyNeurology

Partners

Swedish Orphan Biovitrum (Sobi)
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