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C. Frank Bennett

Executive Vice President, Chief Scientific Officer

Ionis Pharmaceuticals

Ionis Pharmaceuticals Pipeline

DrugIndicationPhase
TRYNGOLZA (olezarsen)Familial Chylomicronemia Syndrome (FCS)Approved
Olezarsen sNDASevere HypertriglyceridemiaNDA Review
DAWNZERA (donidalorsen)Hereditary AngioedemaPhase 3
Vitravene (fomivirsen)CMV-induced retinitisApproved
SPINRAZA (nusinersen)Spinal Muscular AtrophyApproved