PR

Peter Reikes

Incoming Board Member

Ionis Pharmaceuticals

Ionis Pharmaceuticals Pipeline

DrugIndicationPhase
TRYNGOLZA (olezarsen)Familial Chylomicronemia Syndrome (FCS)Approved
Olezarsen sNDASevere HypertriglyceridemiaNDA Review
DAWNZERA (donidalorsen)Hereditary AngioedemaPhase 3
Vitravene (fomivirsen)CMV-induced retinitisApproved
SPINRAZA (nusinersen)Spinal Muscular AtrophyApproved