Sodium phenylbutyrate

Phase 2Recruiting
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Interest: 36/100
36
Hype Score

Development Stage

Pre-clinical
Phase 1
3
Phase 2
4
Phase 3
5
Approved
Indication / Disease

Medium-chain Acyl-CoA Dehydrogenase Deficiency

Conditions

Medium-chain Acyl-CoA Dehydrogenase Deficiency

Trial Timeline

Jun 30, 2025 → Jul 1, 2027

About Sodium phenylbutyrate

Sodium phenylbutyrate is a phase 2 stage product being developed by Zevra Therapeutics for Medium-chain Acyl-CoA Dehydrogenase Deficiency. The current trial status is recruiting. This product is registered under clinical trial identifier NCT06773026. Target conditions include Medium-chain Acyl-CoA Dehydrogenase Deficiency.

Hype Score Breakdown

Clinical
12
Activity
15
Company
9
Novelty
0
Community
0

Clinical Trials (2)

NCT IDPhaseStatus
NCT07125066Phase 1Recruiting
NCT06773026Phase 2Recruiting

Competing Products

2 competing products in Medium-chain Acyl-CoA Dehydrogenase Deficiency

See all competitors
ProductCompanyStageHype Score
TriheptanoinUltragenyx PharmaceuticalPhase 2
36
TriheptanoinUltragenyx PharmaceuticalPhase 2
33