BH4

ApprovedUNKNOWN
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82
Hype Score

Development Stage

โœ“
Pre-clinical
โœ“
Phase 1
โœ“
Phase 2
โœ“
Phase 3
5
Approved
Indication / Disease

Pku Phenylketonuria

Conditions

Pku Phenylketonuria, PAH Deficiency

Trial Timeline

Jun 1, 2020 โ†’ Jun 1, 2022

About BH4

BH4 is a approved stage product being developed by BioMarin Pharmaceutical for Pku Phenylketonuria. The current trial status is unknown. This product is registered under clinical trial identifier NCT04227080. Target conditions include Pku Phenylketonuria, PAH Deficiency.

Hype Score Breakdown

Clinical
30
Activity
20
Company
7
Novelty
10
Community
12

Clinical Trials (1)

NCT IDPhaseStatus
NCT04227080ApprovedUNKNOWN

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