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NM

Natalie Mount, Ph.D.

Executive Vice President, Program & Portfolio Management

MeiraGTx

MeiraGTx Pipeline

DrugIndicationPhase
botaretigene sparoparvovec (bota-vec, AAV-RPGR)X-linked retinitis pigmentosa (XLRP)Phase 3
AAV-CNGB3Achromatopsia (CNGB3-associated)Phase 1/2
AAV-CNGA3Achromatopsia (CNGA3-associated)Phase 1/2
AAV-AQP1Radiation-induced xerostomiaPhase 1
AAV-GADParkinson's DiseasePreclinical/Phase 1
AAV-UPF1Amyotrophic Lateral Sclerosis (ALS)Preclinical