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FP

Frederick Porter, Ph.D.

Chief Technical Officer

Taysha Gene Therapies

Taysha Gene Therapies Pipeline

DrugIndicationPhase
TSHA-102Rett SyndromePhase 1/2
TSHA-120Giant Axonal Neuropathy (GAN)Phase 1/2
TSHA-101GM2 Gangliosidosis (Tay-Sachs/Sandhoff)Preclinical
TSHA-103SLC6A1-related disorderPreclinical
TSHA-104SURF1-associated Leigh syndromePreclinical
TSHA-105FOXG1 syndromePreclinical
TSHA-106SCN8A-related disorderPreclinical
TSHA-107SYNGAP1-related disorderPreclinical