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DA

Dr. Allan R. Martin

Co-Founder

ReGenX Biosciences

ReGenX Biosciences Pipeline

DrugIndicationPhase
RGX-121Mucopolysaccharidosis Type II (MPS II, Hunter syndrome)Phase 2/3
RGX-314Wet Age-Related Macular Degeneration (AMD)Phase 2/3
RGX-202Duchenne Muscular Dystrophy (DMD)Phase 1/2
RGX-381Ocular Manifestations of Fabry DiseasePreclinical