NTLA-2001

Phase 1Completed
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28
Hype Score

Development Stage

โœ“
Pre-clinical
2
Phase 1
3
Phase 2
4
Phase 3
5
Approved
Indication / Disease

Transthyretin-Related (ATTR) Familial Amyloid Polyneuropathy

Conditions

Transthyretin-Related (ATTR) Familial Amyloid Polyneuropathy, Transthyretin-Related (ATTR) Familial Amyloid Cardiomyopathy, Wild-Type Transthyretin Cardiac Amyloidosis

Trial Timeline

Nov 5, 2020 โ†’ Sep 12, 2025

About NTLA-2001

NTLA-2001 is a phase 1 stage product being developed by Intellia Therapeutics for Transthyretin-Related (ATTR) Familial Amyloid Polyneuropathy. The current trial status is completed. This product is registered under clinical trial identifier NCT04601051. Target conditions include Transthyretin-Related (ATTR) Familial Amyloid Polyneuropathy, Transthyretin-Related (ATTR) Familial Amyloid Cardiomyopathy, Wild-Type Transthyretin Cardiac Amyloidosis.

Hype Score Breakdown

Clinical
10
Activity
5
Company
5
Novelty
3
Community
2

Clinical Trials (1)

NCT IDPhaseStatus
NCT04601051Phase 1Completed