LUM001 (Maralixibat)

Phase 2Completed
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49
Hype Score

Development Stage

Pre-clinical
Phase 1
3
Phase 2
4
Phase 3
5
Approved
Indication / Disease

Alagille Syndrome

Conditions

Alagille Syndrome

Trial Timeline

Mar 16, 2015 → Jun 1, 2020

About LUM001 (Maralixibat)

LUM001 (Maralixibat) is a phase 2 stage product being developed by Mirum Pharmaceuticals for Alagille Syndrome. The current trial status is completed. This product is registered under clinical trial identifier NCT02117713. Target conditions include Alagille Syndrome.

Hype Score Breakdown

Clinical
17
Activity
12
Company
7
Novelty
5
Community
5

Clinical Trials (3)

NCT IDPhaseStatus
NCT02117713Phase 2Completed
NCT02057718Phase 2Completed
NCT02047318Phase 2Completed

Competing Products

9 competing products in Alagille Syndrome

See all competitors
ProductCompanyStageHype Score
Odevixibat + PlaceboIpsenPhase 3
74
OdevixibatIpsenPhase 3
74
maralixibatMirum PharmaceuticalsPre-clinical
20
Livmarli + LivmarliMirum PharmaceuticalsPre-clinical
20
LUM001 (Maralixibat)Mirum PharmaceuticalsPhase 2
49
LUM001 (Maralixibat) + PlaceboMirum PharmaceuticalsPhase 2
49
Livmarli Oral ProductMirum PharmaceuticalsApproved
82
LUM001 + PlaceboMirum PharmaceuticalsPhase 2
49
LUM001 + PlaceboMirum PharmaceuticalsPhase 2
49