Deflazacort

Phase 3Terminated
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74
Hype Score

Development Stage

โœ“
Pre-clinical
โœ“
Phase 1
โœ“
Phase 2
4
Phase 3
5
Approved
Indication / Disease

Limb-Girdle Muscular Dystrophy

Conditions

Limb-Girdle Muscular Dystrophy

Trial Timeline

Oct 31, 2019 โ†’ Jan 1, 2021

About Deflazacort

Deflazacort is a phase 3 stage product being developed by PTC Therapeutics for Limb-Girdle Muscular Dystrophy. The current trial status is terminated. This product is registered under clinical trial identifier NCT03783923. Target conditions include Limb-Girdle Muscular Dystrophy.

Hype Score Breakdown

Clinical
27
Activity
18
Company
7
Novelty
9
Community
10

Clinical Trials (8)

NCT IDPhaseStatus
NCT02592941Pre-clinicalCompleted
NCT03783923Phase 3Terminated
NCT03642145Phase 3Withdrawn
NCT02485431Phase 1Completed
NCT02251600Phase 1Completed
NCT02295748Phase 1Completed
NCT02286609Phase 1Completed
NCT02286622Phase 1Completed

Competing Products

3 competing products in Limb-Girdle Muscular Dystrophy

See all competitors
ProductCompanyStageHype Score
SRP-9005 + CorticosteroidSarepta TherapeuticsPhase 3
72
SRP-9003 + GlucocorticoidSarepta TherapeuticsPhase 3
72
ATYR1940 + PlaceboaTyr PharmaPhase 1/2
33