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Yoshihisa Nakagawa

Director and Managing Executive Officer

Nippon Shinyaku

Nippon Shinyaku Pipeline

DrugIndicationPhase
Viltepso (viltolarsen)Duchenne Muscular Dystrophy (exon 53 amenable)Approved
NS-089/NCNP-02Duchenne Muscular Dystrophy (exon 44 amenable)Phase 3
NS-080/NCNP-01Duchenne Muscular Dystrophy (exon 45 amenable)Phase 1/2
Fostamatinib (TAK-632/R788)Immune Thrombocytopenia (ITP)Approved
Miglustat (Brazaves)Niemann-Pick disease type CApproved
NS-0100Undisclosed OncologyPreclinical
NS-0200Undisclosed Rare DiseasePreclinical