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Nicholas Johnson, M.D., M.Sci., FAAN

Scientific Advisor, Armas Family Professor at Virginia Commonwealth University

PepGen

PepGen Pipeline

DrugIndicationPhase
PGN-EDODM1Myotonic Dystrophy Type 1 (DM1)Phase 2
PGN-EDO51Duchenne Muscular Dystrophy (amenable to exon 51 skipping)Phase 2
EDO Platform for CMT1ACharcot-Marie-Tooth disease type 1A (CMT1A)Preclinical
Discovery ProgramsAdditional Neuromuscular & Neurological IndicationsDiscovery