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MO

Michele Oshman

Board Member

Amicus Therapeutics

Amicus Therapeutics Pipeline

DrugIndicationPhase
Galafold (migalastat)Fabry disease (amenable mutations)Approved
Pombiliti (cipaglucosidase alfa) + Opfolda (miglustat)Late-onset Pompe diseaseApproved
AT-GTX-501CLN6 Batten diseasePhase 1/2
AT-GTX-502CLN3 Batten disease (Juvenile)Preclinical
AT-GTX-503CLN1 Batten disease (Infantile)Preclinical