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KS

Kazutaka Shimoda

Director, Managing Executive Officer, Head of Research & Development

JCR Pharmaceuticals

JCR Pharmaceuticals Pipeline

DrugIndicationPhase
IZCARGO® (pabinafusp alfa)Mucopolysaccharidosis II (Hunter syndrome)Approved
JR-141 (pabinafusp alfa)Mucopolysaccharidosis II (Hunter syndrome)Phase 3
JR-171 (lepunafusp alfa)Mucopolysaccharidosis I (with CNS involvement)Phase 1/2
JR-441Sanfilippo syndrome Type A (MPS IIIA)Preclinical
JR-161Tay-Sachs/Sandhoff diseasePreclinical