AV

Akshay Vaishnaw

President

Alnylam Pharmaceuticals

Alnylam Pharmaceuticals Pipeline

DrugIndicationPhase
Patisiran (ONPATTRO)Hereditary Transthyretin AmyloidosisApproved
Givosiran (GIVLAARI)Acute Hepatic PorphyriaApproved
Lumasiran (OXLUMO)Primary Hyperoxaluria Type 1Approved
Inclisiran (LEQVIO)HypercholesterolemiaApproved
VutrisiranHereditary Transthyretin AmyloidosisPhase 3
ALN-AGT01HypertensionPhase 1
ALN-KHKPrimary HyperoxaluriaPhase 3
ALN-APPAlzheimer's DiseasePhase 1