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Undisclosed PRAM (CDKL5-targeting)

CDKL5 Deficiency Disorder

PreclinicalDiscovery

Key Facts

Indication
CDKL5 Deficiency Disorder
Phase
Preclinical
Status
Discovery
Company

About CAMP4 Therapeutics

CAMP4 Therapeutics is developing a new class of therapeutics that modulate gene expression by targeting the regulatory RNA network, a layer of biology upstream of proteins. The company's platform identifies druggable regRNA nodes to design oligonucleotide-based medicines that can precisely tune gene activity. With a focus on haploinsufficiency diseases, where increasing the output of a single healthy gene copy could provide therapeutic benefit, CAMP4 is building a pipeline with initial programs in CNS and metabolic disorders. The company is backed by leading life science investors and is advancing its lead programs toward clinical development.

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