Evrysdi
Spinal muscular atrophy
CommercialActive
Key Facts
About Royalty Pharma
Founded in 1996, Royalty Pharma pioneered the royalty pharma asset class by providing non-dilutive capital to pharmaceutical innovators. The company has deployed over $19 billion to acquire royalty interests in leading medicines across multiple therapeutic areas. As a publicly-traded company on NASDAQ, Royalty Pharma generates revenue from royalty payments on successful drugs while helping fund the next generation of medical breakthroughs.
View full company profileOther Spinal muscular atrophy Drugs
| Drug | Company | Phase |
|---|---|---|
| GYM329 | Chugai Pharmaceutical | Phase 2 |
| Spinraza | Royalty Pharma | Commercial |
| Spinal Muscular Atrophy Program | Biogen | Commercial |
| ASO Candidates for SMA | Biogen | Pre-clinical |
| SPINRAZA (nusinersen) | Ionis Pharmaceuticals | Approved |