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Compact Type II CRISPR System

CNS gene knockdown via AAV delivery

ResearchActive

Key Facts

Indication
CNS gene knockdown via AAV delivery
Phase
Research
Status
Active
Company

About Metagenomi

Metagenomi is pioneering a new era of genetic medicine by harnessing the vast diversity of microbial life through metagenomics to discover and engineer next-generation genome editing tools. Founded by pioneers in the field, the company has built an industry-leading database, identified over 20,000 editing systems, and is advancing a pipeline of in vivo therapies for genetic diseases. With a strong leadership team, strategic partnerships, and a public listing, Metagenomi is positioned to expand its therapeutic reach and translate its novel platform into transformative patient cures.

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