Home/PTC Therapeutics/Jerome B. Zeldis
JB

Jerome B. Zeldis

Independent Board Director

PTC Therapeutics

Roles

Independent Board DirectoratPTC Therapeutics
DirectoratSoligenix

PTC Therapeutics Pipeline

DrugIndicationPhase
Evrysdi (risdiplam)Spinal Muscular Atrophy (SMA)Approved
Translarna (ataluren)Duchenne muscular dystrophy (nmDMD)Approved
Upstaza (eladocagene exuparvovec)Aromatic L-amino acid decarboxylase (AADC) deficiencyApproved
PTC518Huntington's diseasePhase 2
Vatiquinone (PTC743)Friedreich's ataxiaPhase 3
Utreloxastat (PTC857)Amyotrophic Lateral Sclerosis (ALS)Phase 2
PTC923Phenylketonuria (PKU)Phase 3