OCU410ST (AAV5-hRORA)
Stargardt Disease
Phase 2/3Active
Key Facts
About Ocugen
Ocugen is a clinical-stage biotech focused on developing transformative gene therapies for blindness diseases, with a lead program in Phase 3 for retinitis pigmentosa. The company leverages a unique modifier gene therapy platform designed to address multiple genetic mutations with a single treatment, offering a potential paradigm shift in ophthalmology. Ocugen also maintains a portfolio of inhaled vaccines and biologics, supported by strategic partnerships with Bharat Biotech and CanSinoBIO. The company is led by a seasoned team with deep experience in biopharmaceutical development and commercialization.
View full company profileTherapeutic Areas
Other Stargardt Disease Drugs
| Drug | Company | Phase |
|---|---|---|
| Tinlarebant (LBS-008) | Belite Bio | Phase 3 |
| ABO-504 | Abeona Therapeutics | Preclinical |