Home/Pipeline/Alidornase alfa (PRX-110)

Alidornase alfa (PRX-110)

Cystic Fibrosis

Phase 1Completed

Key Facts

Indication
Cystic Fibrosis
Phase
Phase 1
Status
Completed
Company

About Protalix BioTherapeutics

Protalix BioTherapeutics leverages its unique plant cell culture platform, ProCellEx®, to develop recombinant proteins with potential advantages in cost, scalability, and safety. Its flagship product, Elelyso®, is an FDA-approved treatment for Gaucher disease, providing a validated commercial foundation. The company is actively expanding its pipeline, with promising candidates like pegunigalsidase alfa (PRX-102) for Fabry disease in late-stage development, and is exploring strategic partnerships to maximize the platform's potential across multiple therapeutic areas.

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